Genetic Therapy for Dravet Syndrome: 2022 State of the Field
When the Dravet Syndrome Foundation was established in 2009, there were no specific treatments for patients with Dravet syndrome and limited guidelines on best treatment approaches. Despite the known genetic cause for the majority of cases, mutations in SCN1A, the idea of a genetic-based therapy seemed a distant possibility at that time. Things have changed …
Genetic Therapy for Dravet Syndrome: 2022 State of the Field Read More »